Rare Disease Day Freiburg | Webinar | 26 February 2021
Rare Disease Day webinar presented by Freiburg Centre for Rare Diseases on 26th February 2021 from 15:00 – 17:15.
Rare Disease Day Freiburg | Webinar | 26 February 2021 Read More »
innovation projects in clinical trials methodologies
In the context of the EJP RD internal call for innovation projects in clinical trials methodologies in limited populations, that opened on 7th of December 2020 and will close on 3rd of March 2021, an “Information/Networking Event” will be organised on the 25th of January 2021. The meeting will take place online from 15:00 to 18:30.
innovation projects in clinical trials methodologies Read More »
Manifesto for a European Health Union
New manifesto outlines five key goals for establishing a European Health Union to enhance healthcare solidarity and patient protection.
Manifesto for a European Health Union Read More »
Kawasaki Disease Coronary Artery Aneurysm Prevention Trial
First European trial site opens at Great Ormond Street Hospital to study prevention of coronary artery aneurysms in Kawasaki Disease.
Kawasaki Disease Coronary Artery Aneurysm Prevention Trial Read More »
MPS Expert Webinar | GENE THERAPY CTs FOR MPS TYPE III
MPS Expert Webinar | GENE THERAPY CTs FOR MPS TYPE III July 21th 2021.
MPS Expert Webinar | GENE THERAPY CTs FOR MPS TYPE III Read More »
IRDIRC Orphan Drug Development Guidebook
The commentary ‘Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook’ has been published in Nature Reviews
IRDIRC Orphan Drug Development Guidebook Read More »
New Free-to-View Live Webinars | May – June 2020
Enhancing the Quality of Life of Persons Affected by Mucopolysaccharide Across Europe. By taking a multidisciplinary healthcare team approach we can better understand how to work with colleagues to support patients with MPS with their everyday healthcare needs, as well as by having a better understanding of the latest treatment options.
New Free-to-View Live Webinars | May – June 2020 Read More »
Assistant Professor ‘Preclinical therapies for inherited neurometabolic diseases’
Enthusiastic and ambitious Assistant Professor need at Radboud UMC to perform preclinical therapeutic studies for inherited neurometabolic diseases.
Assistant Professor ‘Preclinical therapies for inherited neurometabolic diseases’ Read More »
PRECEPTORSHIP PROGRAMME ON TREATABLE LYSOSOMAL STORAGE DISEASES (LSDS) – MANAGEMENT AND TREATMENT- SALZBURG, 29TH OF JUNE – 1ST OF JULY 2020
Three-day preceptorship programme offers specialized training in lysosomal storage diseases management for international physicians.
Research Mobility Fellowships and Research Training Workshops
European Joint Programme on Rare Diseases announces funding opportunities for research mobility and specialized training workshops.
Research Mobility Fellowships and Research Training Workshops Read More »
Rare Disease Day 2020: Get involved
Annual international campaign raises awareness about rare diseases and their impact on patients’ lives on February 29, 2020.
Rare Disease Day 2020: Get involved Read More »
MetabERN Publication in Orphanet Journal of Rare Diseases
New research examines availability and accessibility of EMA-approved orphan medicines for hereditary metabolic diseases across Europe.
MetabERN Publication in Orphanet Journal of Rare Diseases Read More »
